DTX401 (pariglasgene brecaparvovec) is a Ultragenyx Pharmaceutical Inc. program in Glycogen Storage Disease Type Ia (GSDIa). Every date links its source.
Indication under review: Glycogen Storage Disease Type Ia (GSDIa). Sponsor: Ultragenyx Pharmaceutical Inc. (RARE). Market-cap tier at the time we tracked it: Mid. We track 1 catalyst event for this program: 0 upcoming and 1 in the record. A PDUFA date is the FDA's target date to complete review of a marketing application; a readout is the sponsor's expected date for clinical trial results. What a PDUFA date is · why we do not compare trial results across drugs.
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